Coordination of Care for Patients with Duchenne Muscular Dystrophy: Teamwork is Everything Duchenne Muscular Dystrophy: Speaking with Patients and Families About Advanced Care ...

Muscular dystrophy is a disease caused by mutations in the dystrophin gene. The muscles of muscular dystrophy patients weaken and atrophy over time. Heart and breathing muscles may also eventually be ...

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec, the American Academy of ...

A new gene therapy treatment for Duchenne muscular dystrophy shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in the ...

Yigit Elma, 11, arrives in Abu Dhabi for gene therapy after Turkish community rallies support ...

Scientists have created a new gene therapy for Duchenne muscular dystrophy (DMD) that may not only help stop the disease in DMD patients, but might also help restore their damaged muscles in the ...

Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine Today, the world stands at a crossroads in genetic medicine ...

An 11-year-old boy from Türkiye is receiving care for Elevidys, a one-time gene therapy for Duchenne Muscular Dystrophy (DMD) ...

12-year-old Deklan Locke, who has Duchenne muscular dystrophy, uses a power wheelchair and raises awareness about the disease. Duchenne muscular dystrophy is a rare genetic disorder that causes muscle ...

A drug from the same family licensed for use in patients with Duchenne muscular dystrophy and blood cancer could transform ...

A new gene therapy treatment for Duchenne muscular dystrophy shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in the ...