Korro Bio received U.S. FDA's orphan drug designation for investigational medicine KRRO-110 to treat Alpha-1 Antitrypsin ...

POLG-related diseases disrupt the function of the mitochondria, or "powerhouses" of the cell — starving them of energy.

Prince Frederik of Luxembourg died from a genetic disease called PolG, but experts hope his passing could bring more ...

A young member of the Luxembourg royal family has passed away from a rare genetic disorder affecting his mitochondria.

With thousands of rare diseases affecting millions of families worldwide, one Tampa Bay lawmaker is taking action to position ...

Affected populations: PFIC is a group of rare genetic diseases that cause progressive liver failure. The exact prevalence of ...

Prince Frederik, 22, was a founder and the creative director of a foundation that raised awareness of POLG disorder.

Johns Hopkins scientists develop mRNA "booster" as potential new way to treat rare genetic diseases marked by too low levels ...

Ensuring every newborn has access to life-saving screening and treatment is both a moral and economic imperative.' ...

Acquired DNA mutations found in the SERPINA1 gene can protect liver cells from damage in patients with alpha-1 antitrypsin ...

The son of Prince Robert of Luxembourg and Princess Julie of Nassau, Prince Frederik, has died in Paris the age of 22 due to ...

A new international study has identified key genetic factors that may protect against Alzheimer’s disease (AD), offering ...