DYNE-101 eased myotonia and led to other functional improvements for people with myotonic dystrophy type 1 (DM1) in a ...

GIVI-MPC, a stem cell therapy for certain types of muscular dystrophy, has been granted orphan drug status for treating ...

Columnist Patrick Moeschen was given an incorrect diagnosis of Becker muscular dystrophy, years before learning he actually ...

A gene-editing therapy may correct a defect in the DYSF gene that drives a form of limb-girdle muscular dystrophy (LGMD), per ...

Capricor's biologics license application for deramiocel (CAP-1002) is draws largely on the Phase 2 HOPE-2 trial and its ...

Columnist Shalom Lim saw elements of his own journey with DMD reflected in the Netflix documentary "The Remarkable Life of ...

Columnist Betty Vertin woke up Christmas Eve scared and anxious at the thought that her youngest son with DMD would soon be unable to walk.

Caregiving for young men with Duchenne isn't easy, but columnist Betty Vertin and her husband have learned to provide care as a team.