WOODBRIDGE – A fundraiser to benefit brave 4-year-old township resident Scarlett Griffith and heighten awareness about the ...

In 2015, NICE said that BioMarin's Vimizim could be used to treat patients with the ultra-rare disease Morquio A syndrome, while real-world data was collected on its efficacy. Now – almost seven ...

More: This internationally recognized NJ doctor is on the frontlines battling rare diseases The Marisa Tufaro Foundation ... in Scarlett’s journey. Morquio A Syndrome affects a child’s ...