Valley parents are racing to find a treatment for their son's progressive genetic disorder that will eventually lead to him ...

Valley parents are racing to find a treatment for their son's progressive genetic disorder that will eventually lead to him ...

Cameron Bennett-Milbourne has a rare genetic condition that involves premature ageing and symptoms more commonly associated ...

Enriquez lives with chronic kidney disease, neurofibromatosis, which causes tumors to form, scoliosis and Raynaud's ...

On the heels of its acquisition by Ocuphire Pharma, Opus is planning next steps for its Leber congenital amaurosis type 5 ...

The new data builds upon previously reported 6- and 12-month positive results from adult patients treated in the same study.