What Is Gene Therapy? Pros, Cons & Examples - Cleveland Clinic
Jun 17, 2025 · It works by replacing a malfunctioning gene, “turning off” a disease-causing gene or giving you a new copy of a gene. Approved gene therapies treat inherited blood, …
Gene therapy | Description, Uses, Examples, & Safety Issues
Nov 28, 2025 · Human gene therapy has been attempted on somatic (body) cells for diseases such as cystic fibrosis, adenosine deaminase deficiency, familial hypercholesterolemia, …
FDA Approved Gene Therapy Examples
Find examples of approved gene therapies in the U.S., when they were approved, and the diseases they were approved for.
Gene therapy - Mayo Clinic
Apr 23, 2024 · The U.S. Food and Drug Administration (FDA) has approved gene therapy products for several conditions, including cancer, spinal muscular atrophy, hemophilia and …
List of gene therapies - Wikipedia
This article contains a list of commercially available gene therapies. Beremagene geperpavec (Vyjuvek): treatment of wounds. [2] Exagamglogene autotemcel (Casgevy): treatment for …
Four Success Stories in Gene Therapy | Scientific American
Nov 1, 2021 · Thanks to that new knowledge and steadfast investigations, gene therapy researchers can now point to a growing list of successful gene therapies. Here are four of the …
Current State of Human Gene Therapy: Approved Products and …
In this section, and in Table 3, our attention will be directed towards the culmination of gene therapy endeavors, namely the assortment of approved human gene therapy products that …
Gene Therapies in Action: A Look at Examples of Successful …
Let’s look at some real-life examples of successful gene therapies in these 4 main categories. Viral vector-based methods use a non-hazardous and non-replicating virus to transfer the DNA …
Gene Therapy Successes - University of Utah
Several promising gene-therapy treatments are under development for cancer. One, a modified version of the herpes simplex 1 virus (which normally causes cold sores) has been shown to …
What Are the Current FDA-Approved Gene Therapies?
Gene therapies offer new possibilities for individuals living with inherited conditions caused by a single faulty gene. These treatments aim to correct or compensate for the genetic defect, …